Sequence 533 (hFraRNAi)

Sequence hFraRNAi
Target	FXN ( Homo sapiens )
Description	Frataxin Ensembl: ENSG00000165060 UniGene: Hs.29978 EntrezGene: 2395 Ensembl Chr9: 70840164 - 70878757 Strand: 1 GO terms: 0004428 0005381 0005739 0006118 0006879 0007268 0009055 0016192
Design	shRNA
Chemistry	RNA
Sequence	(51b) NNGTTCGAACCAACGTGGCCTTTCAAGAGAAGGCCACGTTGGTTCGAACNN
Application	gene silencing
Name	hFraRNAi

References

Intrathecal Injections in Children With Spinal Muscular Atrophy: Nusinersen Clinical Trial Experience. Hache M, Swoboda KJ, Sethna N, Farrow-Gillespie A, Khandji A, Xia S, Bishop KM. J Child Neurol. 2016 Jun;31(7):899-906. PubMed:26823478

Background