Sequence 957 (ISIS-129700 , ISIS 129700)
From Wikisequences
| Sequence ISIS-129700 , ISIS 129700 | |
|---|---|
| Target | none |
| Description | Control |
| Design | MOE gapmer |
| Chemistry | moT*moA*moG*moT*moG*C*G*G*A*C*C*T*A*C*C*moC*moA*moC*moG*moA |
| Sequence | moT*moA*moG*moT*moG*C*G*G*A*C*C*T*A*C*C*moC*moA*moC*moG*moA |
| Application | gene silencing |
| Name | ISIS-129700 , ISIS 129700 |
References
Targeting nuclear RNA for in vivo correction of myotonic dystrophy. Wheeler TM1, Leger AJ, Pandey SK, MacLeod AR, Nakamori M, Cheng SH, Wentworth BM, Bennett CF, Thornton CA. Nature. 2012 Aug 2;488(7409):111-5.
Intrathecal Injections in Children With Spinal Muscular Atrophy: Nusinersen Clinical Trial Experience. Hache M, Swoboda KJ, Sethna N, Farrow-Gillespie A, Khandji A, Xia S, Bishop KM. J Child Neurol. 2016 Jun;31(7):899-906. PubMed:26823478
Comments
Background
